• Understanding Genetics and Your Body
    • Overview of Cells
    • Overview of DNA
    • What is a Gene?
    • Overview of Chromosomes
    • What is a Gene Mutation?
    • Understanding Genetic Disorders
    • Monogenic Disorders
  • Understanding Cell Therapy
    • What is Cell Therapy?
    • Overview of Stem Cells
    • Overview of Hematopoietic Stem Cells (HSCs)
    • What is Hematopoietic Stem Cell Therapy?
  • Understanding Gene Therapy
    • What is Gene Therapy?
    • How is Gene Therapy Delivered?
    • What are the Potential Risks of Gene Therapy?
  • Understanding HSC Gene Therapy
    • The HSC Approach to Gene Therapy
    • How is HSC Gene Therapy Made?
    • What is Conditioning?
    • What is the HSC Gene Therapy Process?
  • Resources
    • Online Resources
    • Glossary
  • Keep Me Informed
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  • Skip to footer
AVROBIO Gene Therapy Education

AVROBIO Gene Therapy Education

AVROBIO Gene Therapy Reference

  • Online Resources
  • Glossary
  • Keep Me Informed

05 Resources

Section 1

Online Resources

Looking for more great information about gene and cell therapy? Check out these online resources:

Information for Patients and
Families About Gene and Cell Therapy

  • American Society of Gene & Cell Therapy (ASGCT)*
  • European Society of Gene & Cell Therapy (ESGCT)*
  • Healing Genes

Advocacy Organizations

  • Alliance for Regenerative Medicine (ARM)*
  • Canadian Organization for Rare Disorders (CORD)
  • Global Genes*
  • EURORDIS*
  • National Organization for Rare Disorders (NORD)*

Information About Clinical Trials

  • ClinicalTrials.gov

* AVROBIO has provided funding to these organization in the past and may do so again in the future. Decisions on funding are not related to any content on this website.

Continue learning in the next section

Section 2

Glossary

Gene therapy uses many specialized terms, words, and concepts that may be new to you. Learning what each term or word means can help you better understand these new concepts. Check out the definitions below for many of the terms and words that appear throughout the website.

Next Section ››

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